Hematopoietic stem cell-targeted neonatal gene therapy reverses lethally progressive osteopetrosis in oc/oc mice

M.K. Johansson, T.J. de Vries, A.M. Schoenmaker, M. Ehinger, A.C. Brun, A. Fasth, S. Karlsson, V. Everts, J. Richter

    Research output: Contribution to JournalArticleAcademicpeer-review

    Original languageUndefined/Unknown
    Pages (from-to)5178-5185
    JournalBlood
    Volume109
    DOIs
    Publication statusPublished - 2007

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